Tag: mouse
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A Revolutionary Gene Editing Breakthrough Offers Hope for Children with Alternating Hemiplegia of Childhood
A Revolutionary Gene Editing Breakthrough Offers Hope for Children with Alternating Hemiplegia of Childhood In vivo prime editing shows remarkable promise in treating a devastating neurological disorder in mouse models, paving the way for a potential one-time gene therapy. For families grappling with Alternating Hemiplegia of Childhood (AHC), a rare and severe neurodevelopmental disorder, the…